eRAM
encyclopedia of Rare Disease Annotation for Precision Medicine
| Disease | mucopolysaccharidosis is |
| Comorbidity | C0007682|cns disorder |
| Sentences | 1 |
| PubMedID- 24278249 | Alternative intrathecal ert clinical trials are ongoing, targeting the cns disorders in patients with mps i, ii and iiia, and require repetitive administration on a regular basis. |
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