eRAM
encyclopedia of Rare Disease Annotation for Precision Medicine
| Disease | mucopolysaccharidosis iii |
| Comorbidity | C0027765|neurological disorder |
| Sentences | 2 |
| PubMedID- 24278249 | These data further support the functional benefits of the raav9 gene delivery, since premature death in mps iiib has been attributed to neurological disorders. |
| PubMedID- 25268803 | These results suggest that cell polarisation and oriented migration defects participate to the neurological disorders associated with sanfilippo syndrome. |
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