PedAM
Pediatric Disease Annotations & Medicines
| Disease | hematopoietic stem cell transplantation |
| Phenotype | C0017205|gaucher disease |
| Sentences | 1 |
| PubMedID- 22786501 | Objectives: to determine the role of hematopoietic stem cell transplantation in people with gaucher disease in relation to: mortality risk associated with the procedure; efficacy in modifying the course of the disease; and arrest or regression of neurological manifestations in neuropathic forms (types 2 and 3). |
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